{"doi":"10.17615/fm1q-nk97","title":"Results of a phase IIa study of VX-809, an investigational CFTR corrector compound, in subjects with cystic fibrosis homozygous for the F508del-CFTR mutation","abstract":"VX-809, a cystic fibrosis transmembrane conductance regulator (CFTR) modulator, has been shown to increase the cell surface density of functional F508del-CFTR in vitro.","journal":"UNC Libraries","year":2020,"id":98909,"datarank":0.0,"base_score":0.0,"endowment":0.0,"self_citation_contribution":0.0,"citation_network_contribution":0.0,"self_endowment_contribution":0.0,"citer_contribution":0.0,"corpus_percentile":null,"corpus_rank":null,"citation_count":31,"citer_count":0,"citers_with_citation_signal":0,"citers_with_endowment":0,"datacite_reuse_total":0,"is_dataset":false,"is_dataset_confidence":0.9572,"is_data_producer":false,"deposit_databanks":null,"is_oa":true,"file_count":0,"downloads":0,"has_version_chain":false,"published_date":"2020-01-01","fair_score":null,"fair_percentile":null,"algorithm_id":"datarank_citation_only_1hop_v6","ranking_scope":"data_only","authors":[{"id":362012,"name":"Michael W. Konstan","orcid":"0000-0002-0557-7277","position":1,"is_corresponding":false},{"id":263850,"name":"Steven M. Rowe","orcid":"0000-0001-9045-0133","position":2,"is_corresponding":false},{"id":487264,"name":"Manfred Ballmann","orcid":"0000-0003-4480-1312","position":3,"is_corresponding":false},{"id":487807,"name":"Laurent Vernillet","orcid":null,"position":4,"is_corresponding":false},{"id":331700,"name":"Jordan Dunitz","orcid":"0000-0002-3348-289X","position":5,"is_corresponding":false},{"id":487265,"name":"Jeffrey Clancy","orcid":"0000-0001-5523-5403","position":6,"is_corresponding":false},{"id":457763,"name":"Preston W. Campbell","orcid":null,"position":7,"is_corresponding":false},{"id":487266,"name":"Inez Bronsveld","orcid":"0000-0001-8877-645X","position":8,"is_corresponding":false},{"id":388551,"name":"Michael S. Schechter","orcid":"0000-0002-8473-3767","position":9,"is_corresponding":false},{"id":380114,"name":"Moira L. Aitken","orcid":null,"position":10,"is_corresponding":false},{"id":487808,"name":"Steve Wisseh","orcid":null,"position":11,"is_corresponding":false},{"id":457756,"name":"Melissa A. Ashlock","orcid":null,"position":12,"is_corresponding":false},{"id":457759,"name":"Frank J. Accurso","orcid":null,"position":13,"is_corresponding":false},{"id":456204,"name":"Richard B. Moss","orcid":"0000-0003-3611-4221","position":14,"is_corresponding":false},{"id":380585,"name":"Joseph M. Pilewski","orcid":"0000-0002-0893-1155","position":15,"is_corresponding":false},{"id":12126,"name":"Manu Jain","orcid":"0000-0003-1534-5629","position":16,"is_corresponding":false},{"id":383735,"name":"Ronald C. Rubenstein","orcid":"0000-0002-3138-4006","position":17,"is_corresponding":false},{"id":391450,"name":"K. De Boeck","orcid":null,"position":18,"is_corresponding":false},{"id":146113,"name":"Martyn C. Botfield","orcid":null,"position":19,"is_corresponding":false},{"id":487809,"name":"Anissa Leonard","orcid":null,"position":20,"is_corresponding":false},{"id":487810,"name":"Henry L. Dorkin","orcid":null,"position":21,"is_corresponding":false},{"id":456201,"name":"Michael Boyle","orcid":"0000-0002-9740-1630","position":22,"is_corresponding":false},{"id":337407,"name":"Scott H. Donaldson","orcid":"0000-0003-4802-0388","position":23,"is_corresponding":false},{"id":437988,"name":"Karen McCoy","orcid":"0000-0002-3483-0905","position":24,"is_corresponding":false},{"id":487811,"name":"Daniel Rosenbluth","orcid":null,"position":25,"is_corresponding":false},{"id":457758,"name":"Peter R. Durie","orcid":null,"position":26,"is_corresponding":false},{"id":487812,"name":"Claudia L Ordoñez","orcid":null,"position":27,"is_corresponding":false},{"id":487267,"name":"Karl Yen","orcid":"0009-0002-2337-2045","position":28,"is_corresponding":false},{"id":383889,"name":"Raouf Amin","orcid":"0000-0002-4942-6024","position":29,"is_corresponding":false},{"id":487806,"name":"G Spencer-Green","orcid":null,"position":0,"is_corresponding":true}],"reference_count":0,"raw_metadata":null,"created_at":"2026-07-18T22:36:58.511143Z","pmid":null,"pmcid":null,"fwci":null,"citation_percentile":null,"influential_citations":0,"oa_status":null,"license":null,"views":0,"total_file_size_bytes":0,"version_count":0,"fair_f":null,"fair_a":null,"fair_i":null,"fair_r":null,"fair_zscore":null,"fair_rationale":null,"fair_model":null,"fair_agent_version":null,"fair_fulltext_source":null,"fair_has_llm":null,"fair_computed_at":null,"clinical_trials":[],"software_tools":[],"db_accessions":[],"linked_datasets":[],"topics":[]}