{"doi":"10.17615/bazj-3394","title":"Gene Therapy: Charting a Future Course—Summary of a National Institutes of Health Workshop, April 12, 2013","abstract":"Recently, the gene therapy field has begun to experience clinical successes in a number of different diseases using various approaches and vectors. The workshop Gene Therapy: Charting a Future Course, sponsored by the National Institutes of Health (NIH) Office of Biotechnology Activities, brought together early and mid-career researchers to discuss the key scientific challenges and opportunities, ethical and communication issues, and NIH and foundation resources available to facilitate further clinical advances.","journal":"UNC Libraries","year":2020,"id":138068,"datarank":0.0,"base_score":0.0,"endowment":0.0,"self_citation_contribution":0.0,"citation_network_contribution":0.0,"self_endowment_contribution":0.0,"citer_contribution":0.0,"corpus_percentile":null,"corpus_rank":null,"citation_count":0,"citer_count":0,"citers_with_citation_signal":0,"citers_with_endowment":0,"datacite_reuse_total":0,"is_dataset":false,"is_dataset_confidence":0.9456,"is_data_producer":false,"deposit_databanks":null,"is_oa":true,"file_count":0,"downloads":0,"has_version_chain":false,"published_date":"2020-01-01","fair_score":null,"fair_percentile":null,"algorithm_id":"datarank_citation_only_1hop_v6","ranking_scope":"data_only","authors":[{"id":80306,"name":"Howard J. Federoff","orcid":"0000-0002-7595-6520","position":1,"is_corresponding":false},{"id":457588,"name":"Luk H. Vandenberghe","orcid":"0000-0002-3508-4924","position":2,"is_corresponding":false},{"id":265976,"name":"Aravind Asokan","orcid":"0000-0001-5563-4877","position":3,"is_corresponding":false},{"id":598782,"name":"Mehrdad Abedi","orcid":"0000-0002-1795-2951","position":4,"is_corresponding":false},{"id":29192,"name":"Laurie Zoloth","orcid":"0000-0001-8751-7261","position":5,"is_corresponding":false},{"id":227919,"name":"Prasad S. Adusumilli","orcid":"0000-0002-1699-2046","position":6,"is_corresponding":false},{"id":599505,"name":"Lawrence J. Prograis","orcid":null,"position":7,"is_corresponding":false},{"id":599506,"name":"Marina O’Reilly","orcid":null,"position":8,"is_corresponding":false},{"id":599507,"name":"Robert Jambou","orcid":null,"position":9,"is_corresponding":false},{"id":316552,"name":"Sanford L. Boye","orcid":"0000-0002-7312-3197","position":10,"is_corresponding":false},{"id":548683,"name":"Paul E. Monahan","orcid":"0000-0003-2110-0740","position":11,"is_corresponding":false},{"id":599508,"name":"Rashmi Gopal-Srivastava","orcid":null,"position":12,"is_corresponding":false},{"id":599509,"name":"Linda Gargiulo","orcid":null,"position":13,"is_corresponding":false},{"id":33772,"name":"Jhanelle E. Gray","orcid":"0000-0003-1304-7062","position":14,"is_corresponding":false},{"id":413757,"name":"Miguel Sena‐Esteves","orcid":"0000-0003-0854-0143","position":15,"is_corresponding":false},{"id":598783,"name":"Yasuhiro Ikeda","orcid":"0000-0002-2970-7304","position":16,"is_corresponding":false},{"id":598784,"name":"Eugene Rosenthal","orcid":"0000-0001-6820-3064","position":17,"is_corresponding":false},{"id":104776,"name":"William G. Wierda","orcid":"0000-0002-7357-270X","position":18,"is_corresponding":false},{"id":339719,"name":"Scott Q. Harper","orcid":"0000-0001-5135-4317","position":19,"is_corresponding":false},{"id":240050,"name":"Ronald G. Crystal","orcid":"0000-0001-6177-6839","position":20,"is_corresponding":false},{"id":240513,"name":"Nabil Ahmed","orcid":"0000-0002-0982-8424","position":21,"is_corresponding":false},{"id":599510,"name":"Maureen E. Montgomery","orcid":null,"position":22,"is_corresponding":false},{"id":84904,"name":"Thomas Weber","orcid":"0000-0003-0617-0417","position":23,"is_corresponding":false},{"id":457037,"name":"Leslie Popplewell","orcid":"0000-0002-8418-2811","position":24,"is_corresponding":false},{"id":535625,"name":"Amy P. Patterson","orcid":null,"position":25,"is_corresponding":false},{"id":268053,"name":"Satiro De Oliveira","orcid":"0000-0002-8181-7316","position":26,"is_corresponding":false},{"id":598785,"name":"Jennifer Keys Adair","orcid":"0000-0001-5843-8185","position":27,"is_corresponding":false},{"id":400561,"name":"William F. Goins","orcid":"0000-0001-7744-9891","position":28,"is_corresponding":false},{"id":522045,"name":"Daniel H. Sterman","orcid":"0009-0004-0170-2722","position":29,"is_corresponding":false},{"id":279332,"name":"Bakhos A. Tannous","orcid":"0000-0001-7062-0684","position":30,"is_corresponding":false},{"id":337777,"name":"Yuman Fong","orcid":"0000-0002-8934-9959","position":31,"is_corresponding":false},{"id":3656,"name":"Donald B. Kohn","orcid":"0000-0003-1840-6087","position":0,"is_corresponding":true}],"reference_count":0,"raw_metadata":null,"created_at":"2026-07-18T23:16:59.449905Z","pmid":null,"pmcid":null,"fwci":null,"citation_percentile":null,"influential_citations":0,"oa_status":null,"license":null,"views":0,"total_file_size_bytes":0,"version_count":0,"fair_f":null,"fair_a":null,"fair_i":null,"fair_r":null,"fair_zscore":null,"fair_rationale":null,"fair_model":null,"fair_agent_version":null,"fair_fulltext_source":null,"fair_has_llm":null,"fair_computed_at":null,"clinical_trials":[],"software_tools":[],"db_accessions":[],"linked_datasets":[],"topics":[]}